Allele-selective lowering of mutant HTT protein by HTT-LC3 linker compounds

Zhaoyang Li, Cen Wang, Ziying Wang, Chenggang Zhu, Jie Li, Tian Sha, Lixiang Ma, Chao Gao, Yi Yang, YiMin Sun, Jian Wang, Xiaoli Sun, Chenqi Lu, Marian Difiglia, Yanai Mei, Chen Ding, Shouqing Luo, Yongjun Dang, Yu Ding, Yiyan Fei, Boxun Lu. Allele-selective lowering of mutant HTT protein by HTT-LC3 linker compounds. Nature, 575(7781):203-209, 2019. [doi]

Abstract

Abstract is missing.